Biomarin
/install biomarin
BioMarin Pharmaceutical
发展历程
- 1997: 在加州成立,创始团队来自UCSF和Genentech
- 1999: 纳斯达克上市,代码BMRN
- 2000s: 专注酶替代疗法(ERT),开发Naglazyme和Aldurazyme
- 2014: Kynamro获批,进入罕见代谢疾病核心市场
- 2017: Voxzogo(软骨发育不全)进入临床试验,成为关键管线
- 2020: Roctavian(血友病A基因疗法)提交上市申请,进入基因治疗领域
- 2021: Voxzogo获FDA批准,年峰值销售预期超$10亿
- 2023: 年营收突破$25亿,首次实现全年盈利
- 2024: 与多家大型药企探讨收购,估值超$150亿
核心业务
酶替代疗法(核心收入来源) + 小分子药物 + 基因疗法(新兴管线),主要面向全球罕见病患者群体
竞争优势
20+年罕见病临床数据积累、FDA孤儿药独占期保护、全球罕见病诊疗网络合作关系、极高转换成本的终身治疗方案
关键指标
2023年营收$25亿+;8款上市药物;全球超25个获批市场;研发投入占收入30%+
故事
罕见病药物定价逻辑独特——BioMarin的某些药物年治疗费用超过$30万美元,但因为患者总数极少(某些疾病全球仅数千例),整体市场规模与传统药物不同,定价策略基于'节省的终身护理成本'而非'研发成本分摊'
- Make sure OpenClaw is installed (local or Docker)
- Run the install command in chat:
/install biomarin - After installation, invoke the skill by name or use
/biomarin - Provide required inputs per the skill's parameter spec and get structured output
What is Biomarin?
BioMarin specializes in rare genetic metabolic diseases with enzyme replacement and gene therapies, holding multiple orphan drug approvals globally. It is an AI Agent Skill for Claude Code / OpenClaw, with 29 downloads so far.
How do I install Biomarin?
Run "/install biomarin" in the OpenClaw or Claude Code chat to install it in one step — no extra setup required.
Is Biomarin free?
Yes, Biomarin is completely free, licensed under MIT-0. You can download, install and use it at no cost.
Which platforms does Biomarin support?
Biomarin is cross-platform and runs anywhere OpenClaw / Claude Code is available (cross-platform).
Who created Biomarin?
It is built and maintained by hanxueyuan (@hanxueyuan); the current version is v1.0.0.