Crispr Therapeutics
/install crispr-therapeutics
CRISPR Therapeutics
发展历程
- 2013: Emmanuelle Charpentier和Emmanuelle de Silva在瑞士创立
- 2015: 与Vertex Pharmaceuticals建立战略合作
- 2016: 10月在纳斯达克上市
- 2018: 启动CTX001(镰状细胞病)临床试验
- 2019: CTX001数据显示治愈率近100%
- 2020: Charpentier获诺贝尔化学奖(CRISPR基因编辑)
- 2023: Casgevy获FDA批准,成为全球首个CRISPR基因编辑疗法
- 2024: 与Vertex扩大合作,推进肿瘤学和自身免疫疾病管线
核心业务
CRISPR基因编辑疗法开发 + 与大型药企(如Vertex)的合作授权收入 + 内部管线推进
竞争优势
CRISPR-Cas9核心专利组合(与Broad Institute交叉授权)、首个获批疗法的临床验证、与Vertex的深度绑定、创始团队的诺贝尔奖声誉
关键指标
Casgevy定价$220万美元/疗程;与Vertex合作获得超$10亿里程碑付款;2024年市值约$50亿
故事
Casgevy是医学史上第一个使用CRISPR'基因剪刀'技术获批的疗法——它从患者体内取出造血干细胞,用CRISPR精确编辑后重新注入患者体内,从根本上治愈了镰状细胞病。治疗只需一次,但定价高达220万美元
- Make sure OpenClaw is installed (local or Docker)
- Run the install command in chat:
/install crispr-therapeutics - After installation, invoke the skill by name or use
/crispr-therapeutics - Provide required inputs per the skill's parameter spec and get structured output
What is Crispr Therapeutics?
CRISPR Therapeutics develops CRISPR-Cas9 gene editing therapies, including FDA-approved Casgevy for sickle cell disease, partnering with Vertex Pharmaceuticals. It is an AI Agent Skill for Claude Code / OpenClaw, with 36 downloads so far.
How do I install Crispr Therapeutics?
Run "/install crispr-therapeutics" in the OpenClaw or Claude Code chat to install it in one step — no extra setup required.
Is Crispr Therapeutics free?
Yes, Crispr Therapeutics is completely free, licensed under MIT-0. You can download, install and use it at no cost.
Which platforms does Crispr Therapeutics support?
Crispr Therapeutics is cross-platform and runs anywhere OpenClaw / Claude Code is available (cross-platform).
Who created Crispr Therapeutics?
It is built and maintained by hanxueyuan (@hanxueyuan); the current version is v1.0.0.